Orphan Drugs “ Empowering Hope : Bridging Gaps With Orphan Drugs ’’.

Abstract

• “The Orphan Drug Designation program assigns orphan designation to medicines and biologics that are designed for the safe and effective treatment, diagnosis, or prevention of uncommon diseases/disorders.


• THE SO-CALLED “ORPHAN DRUGS” ARE MEANT TO CURE ILLNESSES THAT ARE SO UNCOMMON THAT THEIR SPONSORSARE HESITANT TO PURSUE THEM UNDER NORMAL COMMERCIALIZATION GUIDELINES.


• THE DEMAND FOR ECONOMIC FEASIBILITY PREVENTS EVEN PRIORITIES OF RESEARCH INTO THESE DISORDERS.


• THEY WERE DEVELOPED IN REACTION TO PUBLIC HEALTH NEEDS, NOT BY THE PHARMACEUTICAL INDUSTRY FOR ECONOMIC REASONS.


• Developing orphan drugs is a significant challenge for pharmaceutical companies.